Rescuing and Repurposing Drugs: Challenges and Opportunities
Track
:
Track 17: Rare/Orphan Diseases
Program Code:
385
Date:
Wednesday, June 26, 2013
Time:
4:00 PM to 5:30 PM
EST
Location:
205B
CHAIR
:
Cindy Luxhoj Hahn, (SCHSUP), President and CEO, Alagille Syndrome Alliance, United States
Cindy Luxhoj Hahn, MUP, AICP, is President & CEO of the Alagille Syndrome Alliance, a non-profit patient support and advocacy group she founded in 1993. Today she continues to guide the Alliance, serving hundreds of families worldwide through education, advocacy, and research.
SPEAKER
(S):
Ciara Kennedy, PhD,MBA,MSc (SPKNON), Vice President, Operations, Lumena Pharmaceuticals, United States
Dr. Kennedy is Vice-President of Operations at Lumena Pharmaceuticals. In this role she focus on the advancing Lumena's clinical stage programs. Prior to joining Lumena Dr. Kennedy has a strong history in driving programs to key milestones, including NDA approval of SavellaŽ for Fibromyalgia.
Larissa Lapteva, (SPKAGY), Medical Officer, Rare Diseases Program, Office of New Drugs, CDER, FDA, United States
Dr. Larissa Lapteva represents the Rare Disease Program of the Office of New Drugs, CDER, FDA.
John C. McKew, PhD (SPKAGY), Acting Scientific Director, Division of Preclinical Innovation TRND, BrIDGs, National Center for Advancing Translational Sciences (NCATS), United States
Dr. McKew is the Chief of the Therapeutic Development Branch at the National Center for Advancing Translational Sciences (NCATS) at NIH. His responsibilities include developing the Therapeutics for Rare & Neglected Disease program & the Bridging Interventional Development Gaps program.
Description
Drug rescue and repurposing presents an opportunity to spur the drug development process by building upon previous research and development efforts. However, this strategy also has challenges, particularly related to treatments for rare/orphan diseases.